uniQure Announces Successful Gene Therapy Delivery in Animal Model
uniQure recently presented data at the American Society of Gene and Cell Therapy (ASGCT) 20th Annual Meeting in Washington, D.C. on successful repeated hepatic gene delivery with their AAV5 vector following a proprietary immunoadsorption procedure in non-human primates (NHPs). The results described successful sequential transduction with the two reporter transgenes and highlighted the progress made in readministration protocols for AAV gene transfers. Click here to read the full press release from uniQure.
Assisting and Advocating for the Bleeding Disorders Community