BioMarin Announces Gene Therapy Program Updates

The following is an announcement from BioMarin. BioMarin announced an update to the community regarding our ongoing gene therapy clinical trial program in hemophilia A. BioMarin’s investigational gene therapy for hemophilia A has not been approved for use; it is in ongoing clinical trials evaluating its safety and efficacy.Clinical Trial OverviewBioMarin’s investigational gene therapy valoctocogene roxaparvovec is currently […]

When Hemophilia Makes You Feel Different

My son, Jackson, is nearing his 12th birthday. For our family, hemophilia is genetic. so Jackson has been dealing with his diagnosis since birth. We’ve been very open about his bleeding disorder since he was little; sharing and educating our family, friends and teachers. We are fortunate in that he can feel a bleed before […]