Page 16 - HFA_Dateline_2020_Q4_Winter

Exploring the
science behind gene
therapy research

Gene therapy research has the potential to bring an entirely
new option to people with specific genetic conditions.
Many gene therapies are in clinical trials to evaluate the
possible risks and benefits for a range of conditions, including
hemophilia. HemDifferently is here with gene therapy
education, providing accurate information on the basics
and beyond.

Want to stay in-the-know and receive the latest information
to your inbox, including invitations to events?

Scan the QR code now or visit
HemDifferently.com to sign up for updates.

No gene therapies for hemophilia
have been approved for use or
determined to be safe or effective.

© 2020 BioMarin Pharmaceutical Inc. All Rights Reserved. MMRC-GTH-0347 10/20